People

PHD STUDENTS

Daniel Bauersachs

Post mitotic neuronal gene repair, gene therapy technology development and rAAVs for IRF2BPL and SYNGAP1 related disorders.

Louise Bomholtz

Post mitotic neuronal gene repair, gene therapy technology development for IRF2BPL related disorders

Sara del Rey

Stem cell based disease modeling, 3D brain organoids, high content phenotyping, drug screening and drug repurposing towards IRF2BPL related disorders.

SCIENTISTS

Niels Weissbach

Homology independent sequence replacement based gene therapy development for IRF2BPL/NEDAMSS and Huntington’s Disease (postdoctoral researcher)

Post Doctoral Researcher

Somatic cell genome editing technology development – recruitment phase.

Technical Assistance

Stephanie Petzold

Gene editing, stem cells, molecular cloning.

Mandy Gerlach

Stem cells.

Anja Vanessa Kirsch

Stem cells, molecular cloning, stem cell clonal isolation

Joy

Blue Heeler

Rotation students

Krishna Nilesh Patel

AAVs, VLPs development (Student visitor, TX, USA)

Alumni

Ludovica Rigat

The role of microglia in neurodegeneration, integration of microglia into 3D brain organoids.

JOINT RESEARCH COLLABORATIVE INSTITUTIONS (under collaboration research agreements, CRAs)

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University of California San Diego (UCSD)

9500 Gilman Drive, La Jolla, CA 92093-0910, United States, CRA no OIC_SD2020-065

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Center for Gene Therapy, Research Institute at Nationwide Children’s Hospital

700 Children’s Drive, Columbus, Ohio 43205, United States/Next Gen Precision Health, Missouri, United States, CRA no NCH 2020-0002 (00271258 4)

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Genetics, Sanford Research

2301 East 60th Street North, Sioux Falls, South Dakota 57104, United States
Sanford Contract no 2168

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Department of Neurology, Mayo Clinic Jacksonville

4500 San Pablo Road, Jacksonville 32224, United States, CRA ID: 558D6709-B382-4AB9-ACB9-22ACECEA8642

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Nemours Children's Hospital

1600 Rockland Rd., Wilmington, DE, United States
CRA CASE NO. NEMOURS FOUNDATION: Nemours Children’s Hospital, Delaware

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The UNIVERSITY MEDICAL CENTER UTRECHT (UMCU)

Heidelberglaan 100, 3584, CX Utrecht, the Netherlands, CRA V1, November 25th 2021

COLLABORATIVE SERVICE FACILITIES

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